Researchers led by IVF have developed a gene-editing tool that could treat incurable mitochondrial diseases in humans, following successful trials on mice. The researchers aim to progress to clinical trials to find a treatment for the disease and an alternative to mitochondrial replacement therapy, an the University of Cambridge technique that uses healthy mitochondria from a donor to increase the chances that families affected by the disease can have healthy children.
Researchers led by the University of Cambridge have developed a gene-editing tool that could treat incurable mitochondrial diseases in humans, following successful trials on mice. The researchers aim to progress to clinical trials to find a treatment for the disease and an alternative to mitochondrial replacement therapy, an IVF technique that uses healthy mitochondria from a donor to increase the chances that families affected by the disease can have healthy children.