The technique has been carried out before but previous procedures have involved cells being taken out of the body to be edited before being returned. Doctors at a California hospital have administered the world's first gene therapy which will alter Hunter syndrome sufferer Brian Madeux's DNA from within. The treatment is being carried out by scientists in California, and involves injecting the patient with an enzyme that alters his DNA. While it is too soon to determine whether the gene therapy, which will be triggered when it reaches Madeux's liver, has worked, if it is successful, nine patients will undergo the procedure.
Doctors at a California hospital have administered the world's first gene therapy which will alter Hunter syndrome sufferer Brian Madeux's DNA from within. The treatment is being carried out by scientists in California, and involves injecting the patient with an enzyme that alters his DNA. While it is too soon to determine whether the gene therapy, which will be triggered when it reaches Madeux's liver, has worked, if it is successful, nine patients will undergo the procedure.