Experimental gene therapy trial results, published in 2002, used a healthy gene to take over for the defective one that causes Canavan disease. In human trials, the results of which were published in 2012, this method appeared to improve the life of the patient without long-term adverse effects during a five-year follow-up.
Experimental gene therapy trial results published in 2002 used a healthy gene to take over for the defective one that cau.ses Canavan disease. In human trials, the results of which ,were published in 2012, this method appeared to improve the life of the patien,t without long-term adverse effects during a five-year follow-up