Kai Chen Na Zhang Jing-Bo Shao Hong Li Jie Li Jia-Ming Xi Wu-Hen Xu Hui Jiang
10.3389/fped.2021.672187
Front Pediatr
2021 Aug 25;9:672187.
curative effect hematopoietic stem cell transplantation infantile refsum disease pex1 zellweger spectrum disorder
CC BY
https://pubmed.ncbi.nlm.nih.gov/34513757/
Case Reports
PMC8424192
34513757
Allogeneic Hematopoietic Stem Cell Transplantation for PEX1-Related Zellweger Spectrum Disorder: A Case Report and Literature Review
2021