Michele Tosi Michela Catteruccia Claudio Cherchi Irene Mizzoni Adele D'Amico
10.36185/2532-1900-077
Acta Myol
2022 Sep 30;41(3):117-120.
onasemnogene abeparvovec risdiplam safety switching therapies
CC BY-NC-ND
https://pubmed.ncbi.nlm.nih.gov/36349185/
Biological Products / therapeutic use Muscular Atrophy, Spinal / therapy Spinal Muscular Atrophies of Childhood / drug therapy
Biological Products / therapeutic use Muscular Atrophy, Spinal / therapy Spinal Muscular Atrophies of Childhood / drug therapy Case Reports Female Genetic Therapy Humans Zolgensma Risdiplam Biological Products
PMC9628802
36349185
Switching therapies: safety profile of Onasemnogene abeparvovec-xioi in a SMA1 patient previously treated with Risdiplam
2022